ISSN 1662-4009 (online)

ey0017.5-3 | Advances in Clinical Practice | ESPEYB17

5.3. Skeletal changes following hematopoietic stem cell transplantation in osteopetrosis

G Shapiro , J Fishleder , P Stepensky , N Simanovsky , V Goldman , R Lamdan

To read the full abstract: J Bone Miner Res. 2020 Apr 24. doi: https://pubmed.ncbi.nlm.nih.gov/32329913/In brief: Hematopoietic stem cell transplantation remains the only curative treatment in children with severe osteopetrosis. According to this study, increased serum calcium and phosphate serve as good markers of successful engraftment, which leads to significant but incomplete n...